Lentiviral vector mediated gene therapy for type I Dent disease ameliorates Dent disease-like phenotypes for three months in ClC-5 null mice.
Yadav MK, Yoo KW, Atala A, Lu B. Lentiviral vector mediated gene therapy for type I Dent disease ameliorates Dent disease-like phenotypes for three months in ClC-5 null mice. Mol Ther Methods Clin Dev. 2022 Dec 08; 27:149-166.